Califano · Clinical cancer research : an official journal of the American Association for Cancer Research 2015 · randomized, double-blind, placebo-controlled phase II trial · n=?

Tadalafil augments tumor specific immunity in patients with head and neck squamous cell carcinoma.

Cited 184 times in the scientific literature.

Level 2 - randomized trial

Randomized, double-blind, placebo-controlled phase II clinical trial.

PubMed 25564570 · doi:10.1158/1078-0432.CCR-14-1716 · record verified 2026-08-27

What was done

A randomized, prospective, double-blind, placebo-controlled phase II clinical trial evaluated the in vivo effects of systemic phosphodiesterase 5 (PDE5) inhibition with tadalafil versus placebo on immune function and myeloid-derived suppressor cells (MDSC) in patients with head and neck squamous cell carcinoma (HNSCC).

What was found

Tadalafil significantly improved immune parameters compared to placebo: - Ex vivo T-cell expansion showed a mean 2.4-fold increase versus 1.1-fold in controls (P = 0.01). - Peripheral MDSC numbers decreased to a mean 0.81-fold change versus a 1.26-fold change in controls (P = 0.001). - General immunity increased as measured by delayed-type hypersensitivity response (P = 0.002). - Tumor-specific immunity in response to HNSCC tumor lysate was augmented (P = 0.04).

Why it matters

This trial demonstrates in humans that the PDE5 inhibitor tadalafil can reverse tumor-mediated immune suppression by reducing MDSC counts and augmenting tumor-specific immunity.

Limits

The abstract does not report the sample size (n), drug dosage, duration of therapy, patient baseline characteristics, or clinical survival endpoints (e.g., progression-free or overall survival).

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