Drzymała-Czyż · European journal of gastroenterology & hepatology 2016 · prospective self-controlled withdrawal trial · n=23

Supplementation of ursodeoxycholic acid improves fat digestion and absorption in cystic fibrosis patients with mild liver involvement.

Cited 17 times in the scientific literature.

Level 3 - non-randomized controlled study

Prospective single-arm interventional withdrawal study with within-subject comparisons

PubMed 26882172 · doi:10.1097/MEG.0000000000000593 · record verified 2026-08-29

What was done

The authors assessed fat digestion and absorption in 23 cystic fibrosis patients with mild liver involvement using a 13C-mixed triglyceride breath test. Testing occurred while patients were taking ursodeoxycholic acid (UDCA) (evaluated without pancreatic enzymes, with standard enzyme doses, and with increased enzyme doses in 16 patients with abnormal initial tests) and again after 1 month of UDCA withdrawal. Cumulative percentage dose recovery (CPDR) served as the measure of lipid absorption.

What was found

Adding standard pancreatic enzymes improved median CPDR from 0% (IQR 0–0) to 4.6% (IQR 0.4–6.0; P < 0.00046). Increasing the enzyme dose in 16 patients with abnormal breath test results further increased CPDR to 8.6% (IQR 5.6–12.7; P < 0.000027). Subsequent withdrawal of UDCA for 1 month resulted in a significant reduction of CPDR to 2.9% (IQR 0.7–5.8; P < 0.000031).

Why it matters

These findings suggest that UDCA improves lipid assimilation alongside pancreatic enzyme replacement therapy in cystic fibrosis patients with liver involvement, highlighting the role of bile acid availability in fat digestion.

Limits

The study had a small sample size (n = 23, with a subgroup of 16) and used an unblinded, non-randomized withdrawal design without a parallel control group. Long-term nutritional endpoints (such as weight gain or growth) were not evaluated, only surrogate breath test kinetics.

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